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Pediatric Beta Thalassemia

Key points about beta thalassemia

  • Beta thalassemia is an inherited blood disorder in which a child has anemia.
  • It is caused by genetic defects that control the production of hemoglobin.
  • The types are beta thalassemia major, intermedia and minor.
  • Treatment includes regular blood transfusions.
  • Treatment for iron overload is needed after years of transfusions.


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Frequently Asked Questions

What is beta thalassemia?

What causes beta thalassemia?

Which children are at risk for beta thalassemia?

What are the symptoms of beta thalassemia?

How is beta thalassemia diagnosed?

How is beta thalassemia major treated?

What are the complications of beta thalassemia?

How can I help my child live with beta thalassemia?

When should I call my child's healthcare provider?

Your Child May Be Eligible for Gene Therapy for Beta Thalassemia

Most patients with beta thalassemia who have received a one-time ZYNTEGLO® treatment have been able to produce sufficient hemoglobin because of the treatment, freeing them from regular blood transfusions.

We Provide Cutting-Edge Treatment

The Children's National Blood and Marrow Transplantation team is a nationally recognized leader in pediatric blood and marrow treatment advances. We are one of the only dedicated pediatric bone marrow transplant programs in the region.


Molly's Story

Providers Who Treat Beta Thalassemia

    Departments that Treat Beta Thalassemia

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    Blood and Marrow Transplant

    Our blood and bone marrow disease experts provide advanced transplant procedures for children and teenagers.